Persons interested in the gene repair therapy that Dr. Blaese spoke to us about at Symposium '98 will want to read the article in the May issue of Fortune magazine titled, "Can Gene Therapy Cure This child?" The article reviews the Kimeragen company's struggle to break into the gene therapy business. It chronicles the problems involved in bringing the therapy to human trials.

The Floyd Martin children from Pennsylvania with Crigler-Najjar Syndrome, are scheduled to be the first to receive the new gene repair therapy.They are featured in the article with a full page photograph of Amy Martin on the first page of the article.

The article is lengthy and very interesting, although MSUD is not mentioned. At Symposium '98 Dr. Blaese told us that children with Mennonite classic MSUD would probably be next in line for trials after the Crigler experiments. This was expected to happen within a couple of years. This article reveals why this hasn't happened yet.The first human trials using this gene repair therapy will be conducted in connection with Dr. Morton's Clinic For Special Children in Strasburg, Pennsylvania. Dr. Blaese will not be able to attend Symposium 2000, so Dr. Holmes Morton will give us an update on the gene repair therapy at that time.


The MSUD Family Support Group is currently funding several research projects and we are proactively looking for researchers interested in developing new treatments or finding a cure for MSUD. Significant funding is necessary if we are to accomplish this goal.
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