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Research

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Acer Therapeutics is developing therapies with established clinical proof-of-concept for the treatment of serious, ultra-rare diseases with critical unmet medical need.
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The Research Trust for Metabolic Diseases in Children.
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MSUD support group in Japan.
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Volume 35-1
23 April 2017

A Message from the Editor

Volume 35-1
23 April 2017

Rare Disease Week 2017

Volume 35-1
23 April 2017

NEWBORN SCREENING LEGISLATION

Transform

A Child's Life

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